SOLVE FSHD is focused on supporting:
- The development, validation and clinical evaluation of biomarkers that predict clinically meaningful outcome measures for use in clinical trials in FSHD.
- Biomarker discovery and Natural History Studies that support drug development efforts.
- Development of pre-clinical systems to increase data quality and success for future therapies advancing to the clinic.
- Development of novel therapies that stop disease progression and / or increase muscle regeneration.